Columnist Betty Vertin, watching her son Chance complete his final season, wishes her sons with DMD could've played football, too.
Treatment with an RNA-based therapy approach was found to correct molecular defects in a cell model of myotonic dystrophy ...
Capricor Therapeutics started its rolling submission seeking FDA approval of its DMD therapy deramiocel for heart muscle ...
The Critical Path Institute will lead a new task force to advance the development of therapies for limb-girdle muscular ...
Columnist Patrick Moeschen has learned to tailor his descriptions of living with limb-girdle muscular dystrophy to his ...
Columnist Betty Vertin, who has seven children, tries to organize the chaos in her family's lives, though no week is typical.
The U.S. Food and Drug Administration (FDA) has granted rare pediatric disease designation to MDL-101, an epigenetic editing therapy that Modalis Therapeutics is developing for LAMA2-related ...
Our house is getting a new piece of medical equipment this week. That’s happened before, as we have three sons with Duchenne muscular dystrophy (DMD): Max, 18, Rowen, 15, and Charlie, 13. Over the ...
Treatment with exon 53-skipping therapy WVE-N531 led to significant increases in muscle dystrophin levels along with signs of improved muscle health and regeneration in boys with Duchenne muscular ...
Our house is getting a new piece of medical equipment this week. That’s happened before, as we have three sons with Duchenne muscular dystrophy (DMD): Max, 18, Rowen, 15, and Charlie, 13. Over the ...
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