Columnist Betty Vertin, watching her son Chance complete his final season, wishes her sons with DMD could've played football, too.
Treatment with an RNA-based therapy approach was found to correct molecular defects in a cell model of myotonic dystrophy ...
Capricor Therapeutics started its rolling submission seeking FDA approval of its DMD therapy deramiocel for heart muscle ...
The Critical Path Institute will lead a new task force to advance the development of therapies for limb-girdle muscular ...
Columnist Patrick Moeschen has learned to tailor his descriptions of living with limb-girdle muscular dystrophy to his ...
A single low dose of the investigational gene therapy BB-301 helped with swallowing for the first two people with oculopharyngeal muscular dystrophy (OPMD) treated in a Phase 1b/2a clinical trial, ...
What’s a typical week as a caregiver of three sons with Duchenne muscular dystrophy (DMD) like? As a primary caregiver to Max, 18, Rowen, 15, and Charlie, 13, my honest answer is that I wish I knew!