Melanie Sanford fought to get her son Hudson a breakthrough gene therapy to stop the progression of the fatal disease ...

Peri Finkelstein, 24, has raised more than $1 million to help children with deadly diseases. She shares her inspiring journey with Fox News Digital, detailing what keeps her motivated to "keep ...

July 24, 2024 — Researchers have made a significant breakthrough in developing a new gene therapy approach that restores full-length dystrophin protein, which could lead to new treatments for ...

A study of 555 patients further solidified genotype-phenotype correlations in Duchenne muscular dystrophy (DMD). A single-center study of 555 individuals with Duchenne muscular dystrophy (DMD ...

Two Chinese biotechs are testing CRISPR gene editing in boys with muscular dystrophy, even as projects at U.S. companies like ...

Capricor Therapeutics is taking a victory lap for their phase 2 Duchenne muscular dystrophy (DMD) trial. | Capricor ...

Duchenne muscular dystrophy (DMD) is a neuromuscular disease causing progressive skeletal muscle weakness and fatigue. The ...

Discover six innovative clinical-stage biotech companies fostering R&D in the Duchenne muscular dystrophy therapeutic space.

Peri Finkelstein isn't letting her disability define her. The MBA grad and advocate has raised more than $1 million to help families with children battling deadly diseases.

Capricor Therapeutics announced promising 3-year results from its HOPE-2 extension study for deramiocel in treating Duchenne ...

Patients with atypical parkinsonism have symptoms like PD, including resting tremors, slowed movement, stiffness, gait difficulty and postural instability, but have additional symptoms and signs that ...

Born with a rare form of muscular dystrophy, Peri Finkelstein has never let her disorder define her. Instead, the 24-year-old New Yorker has used her challenges as a springboard to make the world ...