The agency has reconfirmed its recommendation to not give positive opinion to Translarna (ataluren) after a reexamination of the available data.

The Supreme Court today (Friday) while hearing a plea by a medical candidate suffering from muscular dystrophy observed that ...

In this article, we are going to take a look at where Wave Life Sciences (NASDAQ:WVE) stands against other biggest stocks ...

A dad from York is set to climb Mount Kilimanjaro for his son with muscular dystrophy. Paul McGann, 52, set off for Africa on ...

Muscular Dystrophy Association (MDA) is the #1 voluntary health organization in the United States for people living with muscular dystrophy, ALS, and over 300 related neuromuscular conditions.

Benitec Biopharma Inc.'s positive results for BB-301 in OPMD treatment show promise, but potential risks and financial ...

For the first time this year, the students of McKinley Elementary aided the Muscatine Fire Department in raising money for ...

On Friday 11 October, seven comedians – led by Jon Richardson – came together to entertain an audience of over 1,000 people at Aylesbury Waterside Theatre and raise money for charity.

The three-horse race to treat a devastating form of muscular dystrophy is now down to two. One of the key players, Avidity ...

SAVANNAH, Ga. -- Delandistrogene moxeparvovec (Elevidys), a gene therapy approved to treat Duchenne muscular dystrophy, ...

The father-daughter duo spearheading a new future for muscular dystrophy diseases through the FSHD Global Research Foundation ...