The agency has reconfirmed its recommendation to not give positive opinion to Translarna (ataluren) after a reexamination of the available data.

We recently published a list of 10 Biggest Stocks with Negative Beta to Consider. In this article, we are going to take a ...

Muscular Dystrophy Association (MDA) is the #1 voluntary health organization in the United States for people living with muscular dystrophy, ALS, and over 300 related neuromuscular conditions.

For the first time this year, the students of McKinley Elementary aided the Muscatine Fire Department in raising money for ...

The Supreme Court today (Friday) while hearing a plea by a medical candidate suffering from muscular dystrophy observed that ...

On Friday 11 October, seven comedians – led by Jon Richardson – came together to entertain an audience of over 1,000 people at Aylesbury Waterside Theatre and raise money for charity.

A dad from York is set to climb Mount Kilimanjaro for his son with muscular dystrophy. Paul McGann, 52, set off for Africa on ...

The three-horse race to treat a devastating form of muscular dystrophy is now down to two. One of the key players, Avidity ...

Benitec Biopharma Inc.'s positive results for BB-301 in OPMD treatment show promise, but potential risks and financial ...

SAVANNAH, Ga. -- Delandistrogene moxeparvovec (Elevidys), a gene therapy approved to treat Duchenne muscular dystrophy, ...

The father-daughter duo spearheading a new future for muscular dystrophy diseases through the FSHD Global Research Foundation ...